My son Michele battles daily with a rare genetic disorder known as Duchenne Muscular Dystrophy (DMD). This condition affects all his muscles, taking a significant toll on his quality of life. Currently, steroids serve as the only treatment option. However, the severe side effects associated with these drugs can sometimes outweigh the benefits.

Hope gleams for my son and others in his situation – a drug called Givinostat. Currently pending appraisal and approval under an early access program in the UK, Givinostat offers therapeutic benefits similar to steroids but with significantly fewer side effects.

Nonetheless, the promise of a better life for those affected by DMD depends on legal authorization. We request the responsible bodies to act swiftly and champion the approval of Givinostat. This action would transform lives, allowing those affected by DMD to manage their symptoms effectively while bypassing the harsh side effects associated with steroidal treatments.

Approving Givinostat could mark a turning point in treating DMD, replacing despair with hope. We implore decision-makers to listen to the voices of affected families and to act for the betterment of our loved ones. Please, sign this petition to help ensure that Givinostat gets the approval it needs.