The FDA should be made to approve the first DMD drug, Eteplirsen, by the U.S. Congress.

The Issue

In only one month on May 26th, 2016 the FDA will decide the fate of boys and men with Duchenne.  Eteplirsen is the first drug to treat Duchenne Muscular Dystrophy.  It has no side effects.  The Duchenne patient community along with Physicians around the world that treat Duchenne patients have reported clear increased ability by the children on the drug.  The FDA has refused to accept this as evidence that the drug works. Without this drug thousands of boys will be condemned to wheelchairs in there teens and death in their 20s.   The FDA must be forced by the U.S. Congress to approve Eteplirsen.  

This petition had 6,165 supporters

The Issue

In only one month on May 26th, 2016 the FDA will decide the fate of boys and men with Duchenne.  Eteplirsen is the first drug to treat Duchenne Muscular Dystrophy.  It has no side effects.  The Duchenne patient community along with Physicians around the world that treat Duchenne patients have reported clear increased ability by the children on the drug.  The FDA has refused to accept this as evidence that the drug works. Without this drug thousands of boys will be condemned to wheelchairs in there teens and death in their 20s.   The FDA must be forced by the U.S. Congress to approve Eteplirsen.  

The Decision Makers

Senate Committee on Health, Education, Labor, and Pensions
Senate Committee on Health, Education, Labor, and Pensions

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