Petition update8th Richest County in the World (IsleofMan) denies life changing Duchenne drug Translarna

Is there new hope for Finley? Please help, Thank you.

Clive HeskethOnchan, Isle of Man
Oct 14, 2016
Is there new hope for Finley? Please sign and share to help support our son. PTC Therapeutics announced that the Proceedings of the National Academy of Sciences (PNAS) have published further results to validate Translarna’s (ataluren) mechanism of action. Translarna proposes to promote read-through of premature stop codons which have resulted from nonsense mutations in genetic disorders. The results reported in PNAS validate Ataluren’s ability to alter protein production. It is proposed that Ataluren inserts specific amino acids at premature codons, producing a full-length functional protein.
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