We did it — the FDA heard us. Thank you.

I don't have the words for how grateful I am. On June 17, uniQure announced that after a meeting with the FDA, the agency agreed that the existing 3-year AMT-130 data can serve as the primary basis for an accelerated approval application, with a submission planned for later this year. They also signaled a path that would drop the sham-surgery requirement in the confirmatory study. This is the reversal we fought for.

To the FDA: thank you for listening, and for your commitment to families who have waited far too long for hope.

To our sister HD organizations — the Huntington's Disease Society of America, HD Reach, the Huntington's Disease Foundation, and the Huntington's Disease Youth Organization — thank you for standing shoulder to shoulder with us. This was never one group's fight.

And to this community — the 40,000+ of you who signed, shared, and refused to stay quiet — you are the reason our message could not be ignored. Every signature carried a name, a family, a life.

We're not at the finish line yet. But today, the road ahead looks different than it did before. Thank you for walking it with us.

With gratitude and hope,
Katie Jackson
President/CEO, Help 4 HD International