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Abeona Therapeutics: Give Sanfilippo Kids Access To The Drug That Could Save Their Lives

This petition had 1,173 supporters

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Ryder Belisle has not even had a chance to start his life. He is only 4 years old. He needs your help, to fight his terminal illness, Sanfilippo Syndrome III B. Abeona has said that in the future they should be doing Expanded Access for their Gene Therapy Sanfilippo A and B. You can read their Expanded Access Policy

Here: Abeona's Pre-Approval Process

Ryder is only one of the children who are suffering from Sanfilippo. It is a Rare Disease that occurs in1 in 70,00 for type A and 1 in 200,000 in type B. Many of our children did not qualify for the A and B Clinical Trials with Abeona. This treatment could ultimately save their lives. Sanfilippo is a rapidly progressing terminal disease. Imagine a CHILD having Alzheimer's Disease. They turn into vegetables before your eyes. They can't feed themselves, dress, walk, or talk. The things that people would normally take for granted. Their life expectancy is only in their teens. They were denied this life saving treatment because they were too old or too young, having hearing aids and glasses, an attenuated gene, another illness, etc. I want you for one moment to close your eyes and imagine if this was your child....would you sign?

 We need your SUPPORT to help ask Abeona to do the ethical thing and show some COMPASSION for these children!

Today: Taci is counting on you

Taci Belisle needs your help with “Therapeutics: Abeona Therapeutics: Give Sanfilippo Kids Access To The Drug That Could Save Their Lives”. Join Taci and 1,172 supporters today.